What Is MOTS-c?

MOTS-c is a 16-amino-acid peptide (sequence: MRWQEMGYIFYPRKLR) encoded by a short open reading frame within the mitochondrial 12S ribosomal RNA gene (MT-RNR1). Molecular weight: 2174.6 Da. Highly conserved across 14 species.[1]

Before 2015, MT-RNR1 was considered a structural RNA gene — not a protein-coding region. Its identification as a peptide-hormone source was unexpected, and MOTS-c became one of the first peptides known to originate from the mitochondrial genome rather than the nuclear genome.[1]

The peptide belongs to a class called mitochondrial-derived peptides (MDPs). Two other MDP classes exist: humanin (from the 16S rRNA region, MT-RNR2) and the small humanin-like peptides SHLP1–6 (also from MT-RNR2). MOTS-c is structurally and functionally distinct from both — see MOTS-c vs humanin for the disambiguation.

Endogenous MOTS-c circulates in human plasma. Levels respond to exercise: stationary cycling induced an 11.9-fold increase in skeletal muscle MOTS-c expression and a 1.5–1.6-fold rise in circulating plasma levels in healthy young males, with return toward baseline within four hours post-exercise.[2][3]

What Does MOTS-c Do?

MOTS-c activates AMPK via the folate-AICAR axis. The peptide inhibits the folate cycle and linked de novo purine biosynthesis, causing accumulation of AICAR — an endogenous AMPK activator. Activated AMPK drives increased glucose uptake in skeletal muscle, enhanced fatty acid oxidation, and suppressed hepatic lipid accumulation.[1][17]

Under metabolic stress, MOTS-c translocates from the cytoplasm to the nucleus within 30 minutes in an AMPK-dependent manner, where it interacts with NRF2 and upregulates antioxidant response element (ARE) genes including NQO1 and HO-1.[4]

A 2024 study identified CK2alpha as a direct molecular binding partner for MOTS-c in skeletal muscle. The peptide binds CK2alpha with a dissociation constant of approximately 1 nM, activating it to promote glucose uptake and prevent muscle atrophy.[12]

For the complete MOTS-c mechanism of action, see the research page. The primary tissue targets are skeletal muscle, liver, and adipose tissue. Cardiac, bone, and immune effects have been reported in secondary studies.[10][14][20]

MOTS-c and WADA Prohibition

Note on category: some sources misreport the classification as WADA S2 (Peptide Hormones and Related Substances). The correct category is S4.4.1. This distinction matters for anti-doping proceedings.

USADA confirms MOTS-c has no approved medical use in any jurisdiction as of 2025. No Therapeutic Use Exemption (TUE) pathway exists.

Athletes subject to anti-doping testing must treat MOTS-c as prohibited under all circumstances.

Is MOTS-c Naturally Occurring?

Yes. MOTS-c is an endogenous peptide produced by human mitochondria in skeletal muscle and other tissues. Exercise elevates circulating and intramuscular MOTS-c in healthy adults.[3]

The WADA prohibition applies to the exogenous synthetic analog administered as a research chemical — not to the naturally circulating peptide the body produces. Exogenous and endogenous MOTS-c are structurally identical; the prohibition targets administration, not presence.

MOTS-c in Supplements

USADA warns that MOTS-c may appear in dietary supplements without clear labeling. Athletes should treat any supplement carrying mitochondria-support or AMPK-activator language with caution given the S4.4.1 prohibition and the lack of mandatory pre-market approval requirements for supplements in most jurisdictions.

For MOTS-c side effects and safety signals from the available literature, see the dedicated page.

FDA Approval Status of MOTS-c

REGULATORY STATUS

No FDA-Approved Indication

MOTS-c has no FDA-approved indication. It is not an approved drug in any jurisdiction as of 2025. Compounding pharmacies are prohibited from manufacturing MOTS-c products under FDA guidelines.

CB-4211, a MOTS-c analog developed for obesity, entered early human trials, but peer-reviewed Phase 2 results have not been published. Human interventional trial data for the native 16-amino-acid sequence are absent.

For the full MOTS-c clinical trial status, see the research page.

MOTS-c and TUE Applications

USADA states that MOTS-c has no approved medical use and therefore no TUE would be granted. Athletes subject to anti-doping testing should treat it as prohibited under all circumstances, with no exemption pathway currently available.